AAV GENE THERAPY

A new way to treat disease is on the horizon.

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Leading the Charge

We’re pioneering a new field of discovery

REGENXBIO is seeking to improve lives through the curative potential of gene therapy. Our NAV® Technology Platform has ushered in a new era of gene therapy innovation. 

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Patients & Families

Envisioning a brighter future for patients

We know every day matters to patients and their families. That’s why we are innovating what is possible in gene therapy with the goal of delivering one-time treatments to patients living with common and rare diseases.

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Our NAV® Technology Platform

We are developing gene therapy product candidates in the retinal, metabolic and neurodegenerative therapeutic areas. 

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100+ Novel AAV vectors
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Robust Clinical Programs
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in house commercial-ready manufacturing
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Careers at RegenXBio

Join our team

Awarded Washington Post's Top Work Places in 2021 & 2022

We believe that what we do matters – to patients, to their families and to their communities. We set a high bar for having a culture focused on patients, driven by results, and one that fosters collaboration.  

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