AAV GENE THERAPY

A new way to treat disease is on the horizon.

Img alt
Leading the Charge

We’re pioneering a new field of discovery

REGENXBIO is seeking to improve lives through the curative potential of gene therapy. Our NAV® Technology Platform has ushered in a new era of gene therapy innovation. 

Learn More
Img alt
Patients & Families

Envisioning a brighter future for patients

We know every day matters to patients and their families. That’s why we are innovating what is possible in gene therapy with the goal of delivering one-time treatments to patients living with common and rare diseases.

Learn More

Our NAV® Technology Platform

We are developing gene therapy candidates for rare and retinal diseases. 

differentiator backdrop
100+ Novel AAV vectors
100+ Novel AAV vectors
differentiator backdrop
LATE STAGE CLINICAL PROGRAMS
LATE STAGE CLINICAL PROGRAMS
differentiator backdrop
in house commercial-ready manufacturing
in house commercial-ready manufacturing
Img alt Img alt Img alt Img alt
Careers at RegenXBio

Join our team

Four-Time Winner of Washington Post’s Top Workplaces (2021-2025)

We believe that what we do matters – to patients, to their families and to their communities. We set a high bar for having a culture focused on patients, driven by results, and one that fosters collaboration.  

Learn More