Partners & Licensees Pipeline

Partnering the NAV Technology Platform

PARTNERS & LICENSEES PIPELINE

SORT BY

PROGRAM AREA RESEARCH PRECLINICAL PHASE I/II PHASE III LICENSEE PHASE
Retina

Achromatopsia

PRECLINICAL

Choroideremia

PRECLINICAL
Hematologic/Liver

Citrullinemia Type I

PRECLINICAL

PKU

PRECLINICAL

Wilson Disease

PRECLINICAL

Hemophilia A

PHASE I/II

OTC Deficiency

PHASE I/II

Crigler-Najjar

PHASE I/II

Hemophilia A

PHASE I/II

GSDIa

PHASE I/II
Central Nervous System

Undisclosed

PRECLINICAL

Parkinson’s with GBA

PRECLINICAL

CDKL5 Deficiency

PRECLINICAL

MPS IIIA

PHASE I/II

MPS IIIB

PHASE I/II

CLN3 disease

RESEARCH

CLN1 disease

RESEARCH

ALS SOD1

RESEARCH

ALS SOD1

RESEARCH

MPS IIIA

RESEARCH

SMA Type II

PHASE I/II

SMA Type I

PHASE III

MPS IIIA

PHASE I/II

Rett Syndrome

RESEARCH
Cardiac / Skeletal Muscle

Friedreich’s Ataxia

PRECLINICAL

CPVT

PHASE I/II

XLMTM

PHASE I/II

Pompe Disease

PHASE I/II
Subscribe
REGENXBIO_Logo-RGB

©2018 REGENXBIO Inc. “NAV®” is a registered trademark of REGENXBIO Inc. All rights reserved.

|