ReGenX

Lung

Lung-directed Gene Therapy

Dose

1×1011 GC/mouse.

Volume

0.05 ml

Route of Administration

Intratracheal instillation.

Optimal Serotype(s)

rAAV9

Selected references:

1.    Limberis MP et al.  Transduction efficiencies of novel AAV vectors in mouse airway epithelium in vivo and human ciliated airway epithelium in vitro.  Mol Ther.   17:294-301, 2009.